International collaboration Progress in genetic treatment against rare diseases. Nino Jesus Hospital Tartar is a pathology that participates in a health program Agency prevents from fighting infections, The life expectancy of the affected children is not more than two years of life. Overall, nine children with this condition have been cured after several months of treatment. The case that participated in the Madrid community was a Turkish minor.
“This article shows how to repeat This treatment can cure patients with monogenic diseases Otherwise, in the absence of available hematopoietic tissue donors, they are incurable, ”Dr. Julian Sevilla, the head of the Jessas Hospital’s Hemata and Hemo Therapy, explained,” An American Jesus, the Matal of the University of California, after the child Jesus.
The study is focused on the disease leukocyte adhesion defect 1 (LAD-1). It is made due to the lack of protein called CD 18, its lack Holding white blood cells can go to the bloodstream To fight infections. The result is that the lifespan of the victims, if not receiving this treatment, does not go beyond two years of life, and the lack of functional immune system.
The Administered treatment is in picking stem cells The infected person’s hematopoietics, then introduces them to the functional copy of the defective gene, prevents the body with the production of the CD 18. With this correction, they trigger the patient back. After the 18 to 45 months of administration of this new International Health Milestone, with the cooperation of Madrid’s public health, they all stopped suffering from a series of infections.
In the Madrid community A Turkish Minor has been treated Biomedical Research Center (Ciberr) from the Energy, Environmental and Technical Research Center, with the treatment of professionals of the Health Research Institute of the Health Research Institute of the Jimenez Thiaz Foundation.
